title: Drugs for rare diseases.
mesh_terms: D000818:Animals; D004353:Drug Evaluation, Preclinical; D004345:Drug Industry; D004358:Drug Therapy; D004335:Drug and Narcotic Control; D006527:Hepatolenticular Degeneration / Q000188:drug therapy; D006801:Humans; D051379:Mice; D006113:United Kingdom