Toward enzyme therapy for lysosomal storage diseases.
D002239:Carbohydrate Metabolism, Inborn Errors / Q000188:drug therapy; D004195:Disease Models, Animal; D004341:Drug Evaluation; D004353:Drug Evaluation, Preclinical; D057487:Enzyme Therapy; D004798:Enzymes / Q000008:administration & dosage / Q000276:immunology; D005089:Exocytosis; D005796:Genes; D005809:Genes, Regulator; D008040:Genetic Linkage; D049671:History, 18th Century; D006801:Humans; D006867:Hydrolases / Q000096:biosynthesis; D008052:Lipid Metabolism, Inborn Errors / Q000188:drug therapy; D008247:Lysosomes / Q000201:enzymology* / Q000502:physiology; D008661:Metabolism, Inborn Errors / Q000178:diet therapy / Q000188:drug therapy* / Q000235:genetics; D009154:Mutation; D013106:Sphingolipidoses
D004798:Enzymes; D006867:Hydrolases