Gene therapy for human inherited disorders: techniques and status.
Hoeben
R C
RC
Department of Medical Biochemistry, University of Leiden, The Netherlands.
Valerio
D
D
van der Eb
A J
AJ
van Ormondt
H
H
D000243:Adenosine Deaminase / Q000172:deficiency / Q000235:genetics; D000818:Animals; D004992:Ethics, Medical; D015967:Gene Expression Regulation, Viral; D030342:Genetic Diseases, Inborn / Q000628:therapy*; D015316:Genetic Therapy / Q000379:methods; D005822:Genetic Vectors; D006467:Hemophilia A / Q000235:genetics / Q000628:therapy; D002836:Hemophilia B / Q000235:genetics / Q000628:therapy; D006801:Humans; D008253:Macaca mulatta; D009928:Organ Specificity; D051381:Rats; D012190:Retroviridae / Q000235:genetics / Q000502:physiology; D012192:Retroviridae Infections / Q000517:prevention & control; D012449:Safety; D016511:Severe Combined Immunodeficiency / Q000628:therapy
D000243:Adenosine Deaminase