title: Treatment of patients with severe combined immunodeficiency due to adenosine deaminase (ADA) deficiency by autologous transplantation of genetically modified bone marrow cells.
authors.affiliation: Dept. of Pediatrics, Univ. Hosp. Leiden, The Netherlands.
authors.forename: P M
authors.initials: PM
authors.lastname: Hoogerbrugge
authors.forename: J M
authors.initials: JM
authors.lastname: Vossen
authors.forename: V W
authors.initials: VW
authors.lastname: v Beusechem
authors.forename: D
authors.initials: D
authors.lastname: Valerio
mesh_terms: D000243:Adenosine Deaminase / Q000172:deficiency* / Q000235:genetics; D016026:Bone Marrow Transplantation; D002985:Clinical Protocols; D015316:Genetic Therapy; D006801:Humans; D016511:Severe Combined Immunodeficiency / Q000209:etiology / Q000601:surgery / Q000628:therapy*; D014182:Transplantation, Autologous
chemical_list: D000243:Adenosine Deaminase