Treatment of patients with severe combined immunodeficiency due to adenosine deaminase (ADA) deficiency by autologous transplantation of genetically modified bone marrow cells.
Hoogerbrugge
P M
PM
Dept. of Pediatrics, Univ. Hosp. Leiden, The Netherlands.
Vossen
J M
JM
v Beusechem
V W
VW
Valerio
D
D
D000243:Adenosine Deaminase / Q000172:deficiency* / Q000235:genetics; D016026:Bone Marrow Transplantation; D002985:Clinical Protocols; D015316:Genetic Therapy; D006801:Humans; D016511:Severe Combined Immunodeficiency / Q000209:etiology / Q000601:surgery / Q000628:therapy*; D014182:Transplantation, Autologous
D000243:Adenosine Deaminase