title: Prospects of gene therapy for hemoglobinopathies.
abstract: Gene therapy offers the promise of a definitive cure of the hemoglobinopathies and thalassemias. The background of gene therapy for these disorders is discussed along with the obstacles that must be overcome before this promise becomes reality.
authors.affiliation: Veterans Affairs Medical Center, Jackson, MS 39216.
authors.forename: M H
authors.initials: MH
authors.lastname: Steinberg
mesh_terms: D005544:Forecasting; D005786:Gene Expression Regulation; D005796:Genes; D015316:Genetic Therapy; D005914:Globins / Q000235:genetics; D006453:Hemoglobinopathies / Q000628:therapy*; D006801:Humans; D013789:Thalassemia / Q000628:therapy
chemical_list: D005914:Globins