Prospects of gene therapy for hemoglobinopathies.
Gene therapy offers the promise of a definitive cure of the hemoglobinopathies and thalassemias. The background of gene therapy for these disorders is discussed along with the obstacles that must be overcome before this promise becomes reality.
Steinberg
M H
MH
Veterans Affairs Medical Center, Jackson, MS 39216.
D005544:Forecasting; D005786:Gene Expression Regulation; D005796:Genes; D015316:Genetic Therapy; D005914:Globins / Q000235:genetics; D006453:Hemoglobinopathies / Q000628:therapy*; D006801:Humans; D013789:Thalassemia / Q000628:therapy
D005914:Globins