Gene therapy in man and mice: adenosine deaminase deficiency, ornithine transcarbamylase deficiency, and Duchenne muscular dystrophy.
Grompe
M
M
Institute for Molecular Genetics, Baylor College of Medicine, Houston, TX.
Mitani
K
K
Lee
C C
CC
Jones
S N
SN
Caskey
C T
CT
D000243:Adenosine Deaminase / Q000172:deficiency* / Q000235:genetics; D000592:Amino Acid Metabolism, Inborn Errors / Q000235:genetics / Q000628:therapy; D000818:Animals; D016189:Dystrophin / Q000235:genetics; D015316:Genetic Therapy; D006801:Humans; D008297:Male; D051379:Mice; D009137:Muscular Dystrophy, Animal / Q000235:genetics / Q000628:therapy*; D009954:Ornithine Carbamoyltransferase / Q000235:genetics; D020163:Ornithine Carbamoyltransferase Deficiency Disease; D016511:Severe Combined Immunodeficiency / Q000235:genetics / Q000628:therapy
D016189:Dystrophin; D009954:Ornithine Carbamoyltransferase; D000243:Adenosine Deaminase