Correction of murine mucopolysaccharidosis type VII (MPS VII) by bone marrow transplantation and gene transfer therapy.
Birkenmeier
E H
EH
Jackson Laboratory, Bar Harbor, ME 04609.
D000818:Animals; D016026:Bone Marrow Transplantation; D015316:Genetic Therapy; D005966:Glucuronidase / Q000235:genetics*; D051379:Mice; D016538:Mucopolysaccharidosis VII / Q000235:genetics / Q000628:therapy*; D014162:Transfection
D005966:Glucuronidase