The molecular biology of Gaucher disease and the potential for gene therapy.
Choudary
P V
PV
Tsuji
S
S
Martin
B M
BM
Guild
B C
BC
Mulligan
R C
RC
Murray
G J
GJ
Barranger
J A
JA
Ginns
E I
EI
D000818:Animals; D002460:Cell Line; D005776:Gaucher Disease / Q000235:genetics* / Q000628:therapy; D005796:Genes; D005818:Genetic Engineering / Q000379:methods*; D005822:Genetic Vectors; D005962:Glucosylceramidase / Q000172:deficiency / Q000235:genetics; D006801:Humans; D012190:Retroviridae / Q000235:genetics*; D014158:Transcription, Genetic
D005962:Glucosylceramidase