An appraisal of human trials in enzyme replacement therapy of genetic diseases.
D002986:Clinical Trials as Topic; D057487:Enzyme Therapy; D005733:Gangliosidoses / Q000188:drug therapy; D005776:Gaucher Disease / Q000188:drug therapy; D006009:Glycogen Storage Disease Type II / Q000188:drug therapy; D006596:Hexosaminidases / Q000627:therapeutic use; D006801:Humans; D007068:Iduronidase / Q000627:therapeutic use; D007966:Leukodystrophy, Metachromatic / Q000188:drug therapy; D008099:Liver / Q000378:metabolism; D008661:Metabolism, Inborn Errors / Q000188:drug therapy*; D009083:Mucopolysaccharidoses / Q000188:drug therapy; D000520:alpha-Glucosidases / Q000627:therapeutic use
D006596:Hexosaminidases; D000520:alpha-Glucosidases; D007068:Iduronidase