title: Enzyme replacement therapy by transplantation of HLA-compatible fibroblasts in Sanfilippo A syndrome.
mesh_terms: D002648:Child; D002675:Child, Preschool; D005260:Female; D005347:Fibroblasts / Q000201:enzymology / Q000637:transplantation*; D006025:Glycosaminoglycans / Q000652:urine; D006680:HLA Antigens / Q000276:immunology*; D006801:Humans; D008247:Lysosomes / Q000201:enzymology*; D009083:Mucopolysaccharidoses / Q000628:therapy*; D009084:Mucopolysaccharidosis III / Q000378:metabolism / Q000628:therapy*; D011134:Polysaccharides / Q000032:analysis; D014184:Transplantation, Homologous
chemical_list: D006025:Glycosaminoglycans; D006680:HLA Antigens; D011134:Polysaccharides