Correction of enzyme deficiency in metachromatic leukodystrophy fibroblasts by retroviral-mediated transfer of the human arylsulphatase A gene.
Ohashi
T
T
Department of Pediatrics, Jikei University School of Medicine, Tokyo, Japan.
Eto
Y
Y
Learish
R
R
Barranger
J A
JA
D002553:Cerebroside-Sulfatase / Q000172:deficiency* / Q000235:genetics*; D005347:Fibroblasts / Q000201:enzymology; D015316:Genetic Therapy; D005822:Genetic Vectors; D006801:Humans; D007966:Leukodystrophy, Metachromatic / Q000201:enzymology* / Q000628:therapy*; D012190:Retroviridae / Q000235:genetics*; D014161:Transduction, Genetic
D002553:Cerebroside-Sulfatase