title: A small step for gene therapy.
mesh_terms: D000243:Adenosine Deaminase / Q000172:deficiency / Q000235:genetics / Q000627:therapeutic use; D000328:Adult; D026683:Advisory Committees; D002478:Cells, Cultured; D002648:Child; D002675:Child, Preschool; D003131:Combined Modality Therapy; D028744:Ethics Committees, Research; D035082:Federal Government; D005260:Female; D030342:Genetic Diseases, Inborn; D036281:Genetic Research; D015316:Genetic Therapy / Q000191:economics / Q000331:legislation & jurisprudence; D005914:Globins / Q000172:deficiency / Q000235:genetics / Q000627:therapeutic use; D033161:Government Regulation; D006291:Health Policy; D006801:Humans; D006938:Hyperlipoproteinemia Type II / Q000188:drug therapy / Q000235:genetics / Q000628:therapy*; D008099:Liver; D008148:Lovastatin / Q000627:therapeutic use; D008214:Lymphocytes; D008875:Middle Aged; D011973:Receptors, LDL / Q000172:deficiency / Q000235:genetics*; D011994:Recombinant Proteins / Q000627:therapeutic use; D016511:Severe Combined Immunodeficiency / Q000628:therapy; D017086:beta-Thalassemia / Q000628:therapy
chemical_list: D011973:Receptors, LDL; D011994:Recombinant Proteins; D005914:Globins; D008148:Lovastatin; D000243:Adenosine Deaminase