Gene therapy for cystic fibrosis: challenges and future directions.
Wilson
J M
JM
Institute for Human Gene Therapy, Wistar Institute, Philadelphia, Pennsylvania, 19104, USA.
D000818:Animals; D001692:Biological Transport; D002712:Chlorides / Q000378:metabolism; D003550:Cystic Fibrosis / Q000235:genetics* / Q000503:physiopathology / Q000628:therapy*; D019005:Cystic Fibrosis Transmembrane Conductance Regulator / Q000235:genetics / Q000378:metabolism; D015870:Gene Expression; D005808:Genes, Recessive; D006801:Humans; D008168:Lung / Q000378:metabolism / Q000503:physiopathology; D008954:Models, Biological
C505032:CFTR protein, human; D002712:Chlorides; D019005:Cystic Fibrosis Transmembrane Conductance Regulator