Retroviral-mediated transfer of the iduronate-2-sulfatase gene into lymphocytes for treatment of mild Hunter syndrome (mucopolysaccharidosis type II).
Whitley
C B
CB
University of Minnesota Medical School, Minneapolis, USA.
McIvor
R S
RS
Aronovich
E L
EL
Berry
S A
SA
Blazar
B R
BR
Burger
S R
SR
Kersey
J H
JH
King
R A
RA
Faras
A J
AJ
Latchaw
R E
RE
McCullough
J
J
Pan
D
D
Ramsay
N K
NK
Stroncek
D F
DF
D000328:Adult; D002985:Clinical Protocols; D005240:Feasibility Studies; D018014:Gene Transfer Techniques; D015316:Genetic Therapy; D005822:Genetic Vectors / Q000235:genetics*; D006801:Humans; D007066:Iduronate Sulfatase / Q000235:genetics*; D016532:Mucopolysaccharidosis II / Q000628:therapy*; D012190:Retroviridae / Q000235:genetics*; D013601:T-Lymphocytes
D007066:Iduronate Sulfatase