Development of adeno-associated virus vectors for gene therapy of cystic fibrosis.
Carter
B J
BJ
Targeted Genetics Corporation, Seattle, WA 98101, USA.
Flotte
T R
TR
D000818:Animals; D002460:Cell Line; D002986:Clinical Trials as Topic; D003550:Cystic Fibrosis / Q000628:therapy*; D019005:Cystic Fibrosis Transmembrane Conductance Regulator / Q000235:genetics; D000229:Dependovirus / Q000235:genetics*; D015870:Gene Expression; D015316:Genetic Therapy; D005822:Genetic Vectors; D006801:Humans
C505032:CFTR protein, human; D019005:Cystic Fibrosis Transmembrane Conductance Regulator