Correction of the enzyme deficit of bone marrow cells in congenital erythropoietic porphyria by retroviral gene transfer.
Moreau-Gaudry
F
F
Laboratoire de Biochimie Médicale et Biologie Moléculaire, UPR-ES, Pathologie Moléculaire et Thérapie Génique, Bordeaux, France.
Barbot
C
C
Mazurier
F
F
Mahon
F X
FX
Reiffers
J
J
Ged
C
C
de Verneuil
H
H
D001853:Bone Marrow / Q000201:enzymology*; D002478:Cells, Cultured; D018014:Gene Transfer Techniques; D006801:Humans; D017092:Porphyria, Erythropoietic / Q000201:enzymology / Q000235:genetics*; D011166:Porphyrins / Q000378:metabolism; D012190:Retroviridae; D014576:Uroporphyrinogen III Synthetase / Q000235:genetics* / Q000378:metabolism
D011166:Porphyrins; D014576:Uroporphyrinogen III Synthetase