title: Correction of the enzyme deficit of bone marrow cells in congenital erythropoietic porphyria by retroviral gene transfer.
authors.affiliation: Laboratoire de Biochimie Médicale et Biologie Moléculaire, UPR-ES, Pathologie Moléculaire et Thérapie Génique, Bordeaux, France.
authors.forename: F
authors.initials: F
authors.lastname: Moreau-Gaudry
authors.forename: C
authors.initials: C
authors.lastname: Barbot
authors.forename: F
authors.initials: F
authors.lastname: Mazurier
authors.forename: F X
authors.initials: FX
authors.lastname: Mahon
authors.forename: J
authors.initials: J
authors.lastname: Reiffers
authors.forename: C
authors.initials: C
authors.lastname: Ged
authors.forename: H
authors.initials: H
authors.lastname: de Verneuil
mesh_terms: D001853:Bone Marrow / Q000201:enzymology*; D002478:Cells, Cultured; D018014:Gene Transfer Techniques; D006801:Humans; D017092:Porphyria, Erythropoietic / Q000201:enzymology / Q000235:genetics*; D011166:Porphyrins / Q000378:metabolism; D012190:Retroviridae; D014576:Uroporphyrinogen III Synthetase / Q000235:genetics* / Q000378:metabolism
chemical_list: D011166:Porphyrins; D014576:Uroporphyrinogen III Synthetase