Rare diseases and "orphan" drugs.
B L
BL
Hillcoat
D000328:Adult; D001315:Australia; D002648:Child; D005776:Gaucher Disease / Q000628:therapy; D005962:Glucosylceramidase / Q000627:therapeutic use; D006801:Humans; D009965:Orphan Drug Production / Q000331:legislation & jurisprudence; D011050:Policy Making; D011818:Rabies / Q000188:drug therapy; D011819:Rabies Vaccines / Q000008:administration & dosage; D011994:Recombinant Proteins / Q000627:therapeutic use; D014481:United States; D014486:United States Food and Drug Administration
D011819:Rabies Vaccines; D011994:Recombinant Proteins; D005962:Glucosylceramidase; C090568:imiglucerase