Ribozymes to the rescue: repairing genetically defective mRNAs.
Rossi
J J
JJ
Department of Molecular Biology, Beckman Research Institute of the City of Hope, Duarte, CA 91010-3011, USA. jrossi@coh.org
D000755:Anemia, Sickle Cell / Q000235:genetics / Q000628:therapy; D000818:Animals; D015316:Genetic Therapy; D006801:Humans; D007438:Introns; D009223:Myotonic Dystrophy / Q000235:genetics / Q000628:therapy; D012326:RNA Splicing; D016337:RNA, Catalytic / Q000378:metabolism*; D012333:RNA, Messenger / Q000235:genetics* / Q000378:metabolism*; D016053:RNA, Protozoan / Q000235:genetics / Q000378:metabolism; D013768:Tetrahymena / Q000235:genetics / Q000378:metabolism
D016337:RNA, Catalytic; D012333:RNA, Messenger; D016053:RNA, Protozoan