title: Enzyme replacement therapy in type III Gaucher disease.
authors.affiliation: Department of Metabolic Diseases, Children's Memorial Health Institute, Warsaw, Poland.
authors.forename: A
authors.initials: A
authors.lastname: Tylki-Szymańska
authors.forename: B
authors.initials: B
authors.lastname: Czartoryska
mesh_terms: D000293:Adolescent; D002648:Child; D002675:Child, Preschool; D005776:Gaucher Disease / Q000188:drug therapy*; D005962:Glucosylceramidase / Q000627:therapeutic use*; D006801:Humans; D016896:Treatment Outcome
chemical_list: C070292:alglucerase; D005962:Glucosylceramidase