title: Gaucher's disease: a model for modern management of a genetic disease.
authors.affiliation: Comprehensive Gaucher's Disease Treatment Center, Mount Sinai Medical Center, Mount Sinai School of Medicine, New York, NY 10029-6574, USA. pramod-mistry@smtplink.mssm.edu
authors.forename: P K
authors.initials: PK
authors.lastname: Mistry
mesh_terms: D016026:Bone Marrow Transplantation; D057487:Enzyme Therapy; D005776:Gaucher Disease / Q000150:complications / Q000175:diagnosis / Q000473:pathology / Q000628:therapy*; D015316:Genetic Therapy; D006801:Humans; D016031:Liver Transplantation; D013156:Splenectomy; D004798:Enzymes
chemical_list: D004798:Enzymes