Correction of genetic disease by making sense from nonsense.
Kaufman
R J
RJ
Howard Hughes Medical Institute, University of Michigan Medical School, MSRB II, Room 4570, 1150 West Medical Center Drive, Ann Arbor, Michigan 48109-0650, USA.
D000818:Animals; D018389:Codon, Nonsense / Q000187:drug effects*; D016189:Dystrophin / Q000235:genetics; D030342:Genetic Diseases, Inborn / Q000235:genetics* / Q000378:metabolism / Q000628:therapy*; D015316:Genetic Therapy; D005839:Gentamicins / Q000378:metabolism / Q000494:pharmacology; D006801:Humans; D051379:Mice; D018101:Mice, Inbred mdx; D009137:Muscular Dystrophy, Animal / Q000188:drug therapy / Q000235:genetics / Q000378:metabolism; D009154:Mutation; D012333:RNA, Messenger / Q000235:genetics / Q000378:metabolism
D018389:Codon, Nonsense; D016189:Dystrophin; D005839:Gentamicins; D012333:RNA, Messenger