title: Is there treatment for "genetic" disease?
authors.affiliation: McGill University Health Centre, McGill University-Montreal Children's Hospital Research Institute, Montreal, Canada.
authors.forename: C R
authors.initials: CR
authors.lastname: Scriver
authors.forename: E P
authors.initials: EP
authors.lastname: Treacy
mesh_terms: D000818:Animals; D004195:Disease Models, Animal; D030342:Genetic Diseases, Inborn / Q000628:therapy*; D006801:Humans; D008661:Metabolism, Inborn Errors / Q000628:therapy