Bone marrow transplantation in mucopolysaccharidosis type IIIA: a comparison of an early treated patient with his untreated sibling.
Sivakumur
P
P
Willink Biochemical Genetics Unit, Royal Manchester Children's Hospital, UK.
Wraith
J E
JE
D016026:Bone Marrow Transplantation; D002648:Child; D002675:Child, Preschool; D005260:Female; D006801:Humans; D008297:Male; D009084:Mucopolysaccharidosis III / Q000628:therapy*