Adeno-associated virus-mediated gene transfer of factor IX for treatment of hemophilia B by gene therapy.
Herzog
R W
RW
Department of Pediatrics, University of Pennsylvania Medical Center, Philadelphia, USA.
High
K A
KA
D000818:Animals; D000229:Dependovirus / Q000235:genetics*; D004195:Disease Models, Animal; D005164:Factor IX / Q000235:genetics*; D018014:Gene Transfer Techniques; D015316:Genetic Therapy; D005822:Genetic Vectors; D002836:Hemophilia B / Q000235:genetics / Q000628:therapy*; D006801:Humans; D008099:Liver; D009132:Muscles
D005164:Factor IX