The pathogenesis of cystic fibrosis and progress towards gene therapy.
Stern
M
M
Department of Gene Therapy, Imperial College, National Heart and Lung Institute, London. m.stern@ic.ac.uk
Alton
E
E
D003550:Cystic Fibrosis / Q000235:genetics* / Q000503:physiopathology / Q000628:therapy*; D019005:Cystic Fibrosis Transmembrane Conductance Regulator / Q000235:genetics; D018014:Gene Transfer Techniques; D015316:Genetic Therapy; D006801:Humans; D008957:Models, Genetic
C505032:CFTR protein, human; D019005:Cystic Fibrosis Transmembrane Conductance Regulator