title: Gene therapy trials show clinical efficacy.
authors.forename: J
authors.initials: J
authors.lastname: Stephenson
mesh_terms: D002986:Clinical Trials as Topic; D015316:Genetic Therapy; D006467:Hemophilia A / Q000628:therapy*; D006801:Humans; D016511:Severe Combined Immunodeficiency / Q000628:therapy*