[Therapeutic strategies for peroxisomal disorders].
Therapies are emerging for some of these therapies, and include dietary modification, pharmacological agents, and tissue transplants. Animal models have been developed for several of these disorders, and will increase understanding of disease mechanisms and facilitate the evaluation of current and new therapies, including gene therapy.
Moser
H W
HW
Kennedy Krieger Institute, Baltimore, Maryland, USA.
D000293:Adolescent; D000328:Adult; D002648:Child; D002675:Child, Preschool; D006801:Humans; D007223:Infant; D008875:Middle Aged; D018901:Peroxisomal Disorders / Q000235:genetics / Q000401:mortality / Q000628:therapy*; D015996:Survival Rate