Gene therapy. The best of times, the worst of times.
Anderson
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WF
Norris Cancer Center, Room 6316, University of Southern California, Keck School of Medicine, 1441 Eastlake Avenue, Los Angeles, CA 90033, USA. sdiaz@genome2.hsc.usc.edu
D000243:Adenosine Deaminase / Q000172:deficiency / Q000235:genetics; D018952:Antigens, CD34 / Q000032:analysis; D002318:Cardiovascular Diseases / Q000628:therapy; D002675:Child, Preschool; D002986:Clinical Trials as Topic; D005260:Female; D008040:Genetic Linkage; D015316:Genetic Therapy / Q000009:adverse effects; D005822:Genetic Vectors; D018380:Hematopoietic Stem Cell Transplantation; D006412:Hematopoietic Stem Cells; D006467:Hemophilia A / Q000628:therapy; D006801:Humans; D007223:Infant; D018655:Lymphocyte Count; D018919:Neovascularization, Physiologic; D018123:Receptors, Interleukin / Q000096:biosynthesis / Q000235:genetics*; D016511:Severe Combined Immunodeficiency / Q000201:enzymology / Q000276:immunology / Q000628:therapy*; D013601:T-Lymphocytes / Q000201:enzymology / Q000276:immunology / Q000637:transplantation; D014162:Transfection; D014960:X Chromosome
D018952:Antigens, CD34; D018123:Receptors, Interleukin; D000243:Adenosine Deaminase