Orphan drugs and orphan diseases. Round table proceedings, 3rd European Pediatric Neurology Society Congress. Nice, November 1999.
Campos-Castelló
J
J
University Hospital San Carlos, Servicio de Neuropediatria, Madrid, Spain. jcampos@hcsc.insalud.es
Ponsot
G
G
Feillet
F
F
Vidailhet
M
M
Maire
I
I
D000818:Animals; D002648:Child; D004195:Disease Models, Animal; D004345:Drug Industry / Q000191:economics* / Q000331:legislation & jurisprudence; D004791:Enzyme Inhibitors / Q000627:therapeutic use; D057487:Enzyme Therapy; D005062:European Union; D015316:Genetic Therapy; D006801:Humans; D008661:Metabolism, Inborn Errors / Q000145:classification / Q000175:diagnosis / Q000188:drug therapy* / Q000201:enzymology; D009965:Orphan Drug Production / Q000191:economics / Q000331:legislation & jurisprudence*; D014481:United States
D004791:Enzyme Inhibitors