Gene therapy for lysosomal storage disorders with neuropathology.
Ioannou
Yiannis A
YA
Department of Human Genetics, Gene Therapy and Molecular Medicine, The Mount Sinai School of Medicine, New York, New York.
D000818:Animals; D057487:Enzyme Therapy; D015316:Genetic Therapy; D006801:Humans; D016464:Lysosomal Storage Diseases / Q000150:complications* / Q000628:therapy*; D019636:Neurodegenerative Diseases / Q000209:etiology*; D004798:Enzymes
D004798:Enzymes