Cystic fibrosis gene therapy trials and tribulations.
Johns Hopkins Hospital, Baltimore, Maryland 21287, USA. pzeitli@jhmi.edu
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Zeitlin
D002986:Clinical Trials as Topic; D003550:Cystic Fibrosis / Q000235:genetics / Q000378:metabolism / Q000628:therapy*; D019005:Cystic Fibrosis Transmembrane Conductance Regulator / Q000235:genetics; D015870:Gene Expression; D015316:Genetic Therapy / Q000379:methods*; D006801:Humans; D012333:RNA, Messenger / Q000235:genetics / Q000378:metabolism
C505032:CFTR protein, human; D012333:RNA, Messenger; D019005:Cystic Fibrosis Transmembrane Conductance Regulator