title: Fluorescence-based selection of gene-corrected hematopoietic stem and progenitor cells based on acid sphingomyelinase expression.
authors.affiliation: Department of Human Genetics, Mount Sinai School of Medicine, New York, New York 10029, USA.
authors.forename: E H
authors.initials: EH
authors.lastname: Schuchman
authors.forename: S
authors.initials: S
authors.lastname: Erlich
authors.forename: S R
authors.initials: SR
authors.lastname: Miranda
authors.forename: T
authors.initials: T
authors.lastname: Dinur
authors.forename: A
authors.initials: A
authors.lastname: Dagan
authors.forename: S
authors.initials: S
authors.lastname: Gatt
mesh_terms: D000818:Animals; D001854:Bone Marrow Cells / Q000166:cytology* / Q000187:drug effects; D001896:Boron Compounds; D002469:Cell Separation / Q000379:methods; D002478:Cells, Cultured; D002501:Centrifugation, Zonal / Q000379:methods; D018920:Coculture Techniques; D003114:Colony-Forming Units Assay; D005434:Flow Cytometry / Q000379:methods; D005456:Fluorescent Dyes; D005472:Fluorouracil / Q000494:pharmacology; D018014:Gene Transfer Techniques; D006412:Hematopoietic Stem Cells / Q000166:cytology*; D006801:Humans; D008081:Liposomes; D051379:Mice; D008810:Mice, Inbred C57BL; D018345:Mice, Knockout; D019009:Proto-Oncogene Proteins c-kit / Q000032:analysis; D013108:Sphingomyelin Phosphodiesterase / Q000172:deficiency / Q000235:genetics / Q000378:metabolism*; D013109:Sphingomyelins / Q000378:metabolism
chemical_list: C095489:4,4-difluoro-4-bora-3a,4a-diaza-s-indacene; D001896:Boron Compounds; D005456:Fluorescent Dyes; D008081:Liposomes; D013109:Sphingomyelins; D019009:Proto-Oncogene Proteins c-kit; D013108:Sphingomyelin Phosphodiesterase; D005472:Fluorouracil