Hemophilia. After a setback, gene therapy progresses...gingerly.
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D000818:Animals; D002986:Clinical Trials as Topic; D000229:Dependovirus / Q000235:genetics; D004285:Dogs; D005164:Factor IX / Q000235:genetics; D005169:Factor VIII / Q000235:genetics; D036281:Genetic Research; D015316:Genetic Therapy / Q000009:adverse effects; D005822:Genetic Vectors / Q000008:administration & dosage; D006467:Hemophilia A / Q000235:genetics / Q000628:therapy; D002836:Hemophilia B / Q000235:genetics / Q000628:therapy*; D006801:Humans; D008099:Liver / Q000378:metabolism; D009132:Muscles / Q000378:metabolism; D014481:United States; D014486:United States Food and Drug Administration
D005169:Factor VIII; D005164:Factor IX