title: Treatment of the immune dysregulation, polyendocrinopathy, enteropathy, X-linked syndrome (IPEX) by allogeneic bone marrow transplantation.
authors.affiliation: Service d'Immunologie et d'Hématologie Pédiatriques, H pital Necker-Enfants Malades, Paris, France.
authors.forename: O
authors.initials: O
authors.lastname: Baud
authors.forename: O
authors.initials: O
authors.lastname: Goulet
authors.forename: D
authors.initials: D
authors.lastname: Canioni
authors.forename: F
authors.initials: F
authors.lastname: Le Deist
authors.forename: I
authors.initials: I
authors.lastname: Radford
authors.forename: D
authors.initials: D
authors.lastname: Rieu
authors.forename: S
authors.initials: S
authors.lastname: Dupuis-Girod
authors.forename: N
authors.initials: N
authors.lastname: Cerf-Bensussan
authors.forename: M
authors.initials: M
authors.lastname: Cavazzana-Calvo
authors.forename: N
authors.initials: N
authors.lastname: Brousse
authors.forename: A
authors.initials: A
authors.lastname: Fischer
authors.forename: J L
authors.initials: JL
authors.lastname: Casanova
mesh_terms: D000743:Anemia, Hemolytic / Q000235:genetics / Q000628:therapy*; D001327:Autoimmune Diseases / Q000235:genetics / Q000628:therapy*; D016026:Bone Marrow Transplantation; D004268:DNA-Binding Proteins / Q000235:genetics; D003922:Diabetes Mellitus, Type 1 / Q000235:genetics / Q000628:therapy*; D003967:Diarrhea / Q000235:genetics / Q000628:therapy*; D017809:Fatal Outcome; D005260:Female; D051858:Forkhead Transcription Factors; D008040:Genetic Linkage; D006801:Humans; D007223:Infant; D008297:Male; D010375:Pedigree; D017354:Point Mutation; D016884:Polyendocrinopathies, Autoimmune / Q000235:genetics / Q000628:therapy; D013577:Syndrome; D014184:Transplantation, Homologous; D014960:X Chromosome
chemical_list: D004268:DNA-Binding Proteins; C418974:FOXP3 protein, human; D051858:Forkhead Transcription Factors