Human gene therapy. Harsh lessons, high hopes.
Thompson
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D000293:Adolescent; D002675:Child, Preschool; D017809:Fatal Outcome; D005260:Female; D015316:Genetic Therapy / Q000009:adverse effects / Q000266:history / Q000379:methods / Q000592:standards; D049673:History, 20th Century; D006801:Humans; D008297:Male; D009316:National Institutes of Health (U.S.) / Q000266:history / Q000458:organization & administration; D020163:Ornithine Carbamoyltransferase Deficiency Disease / Q000628:therapy; D011640:Public Policy; D016511:Severe Combined Immunodeficiency / Q000628:therapy; D014481:United States