title: Advances in the treatment of lysosomal storage disease.
authors.affiliation: Willink Biochemical Genetics Unit, Royal Manchester Children's Hospital, UK. ed@willink.demon.co.uk
authors.forename: J E
authors.initials: JE
authors.lastname: Wraith
mesh_terms: D016026:Bone Marrow Transplantation; D057487:Enzyme Therapy; D004798:Enzymes / Q000235:genetics / Q000378:metabolism; D015316:Genetic Therapy; D006801:Humans; D016464:Lysosomal Storage Diseases / Q000201:enzymology* / Q000235:genetics / Q000628:therapy*; D010166:Palliative Care; D011994:Recombinant Proteins / Q000235:genetics / Q000378:metabolism / Q000627:therapeutic use; D013379:Substrate Specificity
chemical_list: D004798:Enzymes; D011994:Recombinant Proteins