Future perspectives for Tay-Sachs disease.
Desnick
R J
RJ
Department of Human Genetics, Mount Sinai School of Medicine of New York University, New York 10029, USA.
Kaback
M M
MM
D000818:Animals; D005817:Genetic Counseling; D006801:Humans; D051379:Mice; D009841:Oligonucleotides / Q000737:chemistry; D011995:Recombination, Genetic; D013234:Stem Cells / Q000378:metabolism; D013661:Tay-Sachs Disease / Q000235:genetics* / Q000517:prevention & control / Q000523:psychology* / Q000628:therapy*
D009841:Oligonucleotides