title: Gene therapy of human disease.
authors.affiliation: Division of Hematology, Department of Molecular and Experimental Medicine, Scripps Research Institute, La Jolla, CA 92037, USA.
authors.forename: Danuta
authors.initials: D
authors.lastname: Balicki
authors.forename: Ernest
authors.initials: E
authors.lastname: Beutler
mesh_terms: D000163:Acquired Immunodeficiency Syndrome / Q000628:therapy; D000818:Animals; D001172:Arthritis, Rheumatoid / Q000628:therapy; D002318:Cardiovascular Diseases / Q000628:therapy; D003550:Cystic Fibrosis / Q000628:therapy; D005776:Gaucher Disease / Q000628:therapy; D018014:Gene Transfer Techniques; D015316:Genetic Therapy; D005822:Genetic Vectors; D006801:Humans; D008661:Metabolism, Inborn Errors / Q000628:therapy; D009369:Neoplasms / Q000628:therapy; D014162:Transfection