title: Designing and characterizing hammerhead ribozymes for use in AAV vector-mediated retinal gene therapies.
authors.affiliation: Department of Molecular Genetics and Microbiology, College of Medicine, University of Florida, Gainesville, Florida 32610, USA.
authors.forename: Jason J
authors.initials: JJ
authors.lastname: Fritz
authors.forename: D Alan
authors.initials: DA
authors.lastname: White
authors.forename: Alfred S
authors.initials: AS
authors.lastname: Lewin
authors.forename: William W
authors.initials: WW
authors.lastname: Hauswirth
mesh_terms: D001483:Base Sequence; D000229:Dependovirus / Q000235:genetics*; D015316:Genetic Therapy; D005822:Genetic Vectors; D008969:Molecular Sequence Data; D009690:Nucleic Acid Conformation; D012313:RNA / Q000737:chemistry; D016337:RNA, Catalytic / Q000235:genetics* / Q000627:therapeutic use; D012172:Retinaldehyde / Q000378:metabolism*
chemical_list: D016337:RNA, Catalytic; D012313:RNA; D012172:Retinaldehyde