Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement.
Aiuti
Alessandro
A
Vai
Sergio
S
Mortellaro
Alessandra
A
Casorati
Giulia
G
Ficara
Francesca
F
Andolfi
Grazia
G
Ferrari
Giuliana
G
Tabucchi
Antonella
A
Carlucci
Filippo
F
Ochs
Hans D
HD
Notarangelo
Luigi D
LD
Roncarolo
Maria Grazia
MG
Bordignon
Claudio
C
D000243:Adenosine Deaminase / Q000008:administration & dosage / Q000172:deficiency* / Q000235:genetics* / Q000378:metabolism / Q000627:therapeutic use*; D000818:Animals; D002417:Cattle; D015316:Genetic Therapy; D006801:Humans; D017710:Lymphocyte Transfusion; D016511:Severe Combined Immunodeficiency / Q000628:therapy*; D013601:T-Lymphocytes / Q000201:enzymology
D000243:Adenosine Deaminase; C051409:pegademase bovine