Gene-based approaches to the treatment of hemophilia.
High
Katherine
K
The Children's Hospital of Philadelphia, 3516 Civic Center Boulevard, Philadelphia, PA 19104, USA. high@email.chop.edu
D005164:Factor IX / Q000235:genetics; D005169:Factor VIII / Q000235:genetics; D005799:Genes, Dominant; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors; D006467:Hemophilia A / Q000235:genetics* / Q000628:therapy*
D005169:Factor VIII; D005164:Factor IX