Gene therapy for SCID--a complication after remarkable progress.
Buckley
Rebecca H
RH
Duke University Medical Center, Durham, NC, USA. buckl003@mc.duke.edu
D000818:Animals; D004195:Disease Models, Animal; D015316:Genetic Therapy / Q000009:adverse effects* / Q000379:methods*; D005822:Genetic Vectors; D018380:Hematopoietic Stem Cell Transplantation / Q000009:adverse effects*; D006801:Humans; D007223:Infant; D016254:Mutagenesis, Insertional; D054198:Precursor Cell Lymphoblastic Leukemia-Lymphoma / Q000209:etiology* / Q000235:genetics; D012190:Retroviridae; D016511:Severe Combined Immunodeficiency / Q000235:genetics / Q000628:therapy*