title: A story of mice and men.
authors.affiliation: Anton McCaffrey and Mark Kay are in the Program in Human Gene Therapy, Departments of Pediatrics and Genetics, Stanford University School of Medicine, Stanford, California 94305, USA.
authors.forename: Anton P
authors.initials: AP
authors.lastname: McCaffrey
authors.forename: Mark A
authors.initials: MA
authors.lastname: Kay
mesh_terms: D000818:Animals; D015316:Genetic Therapy / Q000379:methods*; D006801:Humans; D051379:Mice; D034622:RNA Interference; D014162:Transfection