Lentiviral vectors for gene transfer to the central nervous system. Applications in lysosomal storage disease animal models.
Watson
Deborah J
DJ
Department of Pathobiology, Center for Comparative Medical Genetics, School of Veterinary Medicine, University of Pennsylvania, Department of Neurology and Neuroscience Research, Children's Hospital of Philadelphia, Philadelphia, PA, USA.
Wolfe
John H
JH
D000818:Animals; D001921:Brain; D004195:Disease Models, Animal; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors; D005966:Glucuronidase / Q000378:metabolism; D006801:Humans; D016086:Lentivirus / Q000235:genetics*; D020140:Lysosomal Storage Diseases, Nervous System / Q000235:genetics / Q000378:metabolism / Q000628:therapy*; D014161:Transduction, Genetic
D005966:Glucuronidase