Gene therapy of X-linked severe combined immunodeficiency.
Hacein-Bey-Abina
Salima
S
Gene and Cell Therapy Unit, Institut National de la Santé et de la Recherche Médicale, Hôpital Necker Enfants Malades, Paris, France.
de Saint Basile
Genevieve
G
Cavazzana-Calvo
Marina
M
D016475:3T3 Cells; D000818:Animals; D018952:Antigens, CD34 / Q000276:immunology; D015139:Blotting, Southern / Q000379:methods; D001854:Bone Marrow Cells / Q000276:immunology; D040181:Genetic Diseases, X-Linked / Q000235:genetics / Q000628:therapy*; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors; D006801:Humans; D051379:Mice; D016133:Polymerase Chain Reaction / Q000379:methods; D012190:Retroviridae; D016511:Severe Combined Immunodeficiency / Q000235:genetics / Q000628:therapy*; D014161:Transduction, Genetic / Q000379:methods*
D018952:Antigens, CD34