title: A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency.
authors.forename: Salima
authors.initials: S
authors.lastname: Hacein-Bey-Abina
authors.forename: Christof
authors.initials: C
authors.lastname: von Kalle
authors.forename: Manfred
authors.initials: M
authors.lastname: Schmidt
authors.forename: Françoise
authors.initials: F
authors.lastname: Le Deist
authors.forename: Nicolas
authors.initials: N
authors.lastname: Wulffraat
authors.forename: Elisabeth
authors.initials: E
authors.lastname: McIntyre
authors.forename: Isabelle
authors.initials: I
authors.lastname: Radford
authors.forename: Jean-Luc
authors.initials: JL
authors.lastname: Villeval
authors.forename: Christopher C
authors.initials: CC
authors.lastname: Fraser
authors.forename: Marina
authors.initials: M
authors.lastname: Cavazzana-Calvo
authors.forename: Alain
authors.initials: A
authors.lastname: Fischer
mesh_terms: D048868:Adaptor Proteins, Signal Transducing; D002880:Chromosomes, Human, Pair 11 / Q000235:genetics; D041321:Chromosomes, Human, X; D004268:DNA-Binding Proteins / Q000235:genetics*; D015870:Gene Expression; D008040:Genetic Linkage; D015316:Genetic Therapy / Q000009:adverse effects*; D006801:Humans; D060588:LIM Domain Proteins; D018655:Lymphocyte Count; D008667:Metalloproteins / Q000235:genetics*; D016254:Mutagenesis, Insertional; D054198:Precursor Cell Lymphoblastic Leukemia-Lymphoma / Q000209:etiology*; D011518:Proto-Oncogene Proteins; D012190:Retroviridae; D016511:Severe Combined Immunodeficiency / Q000628:therapy*
chemical_list: D048868:Adaptor Proteins, Signal Transducing; D004268:DNA-Binding Proteins; D060588:LIM Domain Proteins; C085117:LMO2 protein, human; D008667:Metalloproteins; D011518:Proto-Oncogene Proteins