title: 103rd ENMC international workshop: designing rational therapy of SMA based on the understanding of its pathophysiology, 18-20 January 2002, Naarden, The Netherlands.
authors.affiliation: Department of Anatomy and Developmental Biology, University College London, Gower Street, London WC1E 6BT, UK. g.vrbova@ucl.ac.uk
authors.forename: Gerta
authors.initials: G
authors.lastname: Vrbová
authors.forename: Judith
authors.initials: J
authors.lastname: Melki
mesh_terms: D000818:Animals; D002470:Cell Survival / Q000502:physiology; D004195:Disease Models, Animal; D015316:Genetic Therapy; D006801:Humans; D009046:Motor Neurons / Q000502:physiology; D009134:Muscular Atrophy, Spinal / Q000235:genetics / Q000503:physiopathology / Q000628:therapy*; D009154:Mutation; D020511:Neuromuscular Junction Diseases / Q000235:genetics / Q000628:therapy*