title: Clinical trials and rare diseases.
authors.forename: Stephen W
authors.initials: SW
authors.lastname: Lagakos
mesh_terms: D000328:Adult; D000935:Antifungal Agents / Q000627:therapeutic use*; D002648:Child; D003627:Data Interpretation, Statistical; D006105:Granulomatous Disease, Chronic / Q000188:drug therapy*; D006801:Humans; D017964:Itraconazole / Q000627:therapeutic use*; D009181:Mycoses / Q000517:prevention & control; D016032:Randomized Controlled Trials as Topic / Q000379:methods*; D035583:Rare Diseases / Q000628:therapy; D012107:Research Design
chemical_list: D000935:Antifungal Agents; D017964:Itraconazole