title: Home treatment with enzyme replacement therapy in a 5-year-old girl with type 2 Gaucher disease.
authors.affiliation: Department of Pediatrics, Nippon Medical School, Tokyo, Japan. migita-makoto-bmb@nms.ac.jp
authors.forename: Makoto
authors.initials: M
authors.lastname: Migita
authors.forename: Takashi
authors.initials: T
authors.lastname: Shimada
authors.forename: Jun
authors.initials: J
authors.lastname: Hayakawa
authors.forename: Cai Ling
authors.initials: CL
authors.lastname: Zhi
authors.forename: Toshisada
authors.initials: T
authors.lastname: Morita
authors.forename: Kiyohiko
authors.initials: K
authors.lastname: Ohshiro
authors.forename: Yoshitaka
authors.initials: Y
authors.lastname: Fukunaga
mesh_terms: D002675:Child, Preschool; D005260:Female; D005776:Gaucher Disease / Q000188:drug therapy*; D005962:Glucosylceramidase / Q000627:therapeutic use*; D018575:Home Care Services, Hospital-Based; D006801:Humans; D011994:Recombinant Proteins / Q000627:therapeutic use*
chemical_list: D011994:Recombinant Proteins; D005962:Glucosylceramidase; C090568:imiglucerase