Home treatment with enzyme replacement therapy in a 5-year-old girl with type 2 Gaucher disease.
Migita
Makoto
M
Department of Pediatrics, Nippon Medical School, Tokyo, Japan. migita-makoto-bmb@nms.ac.jp
Shimada
Takashi
T
Hayakawa
Jun
J
Zhi
Cai Ling
CL
Morita
Toshisada
T
Ohshiro
Kiyohiko
K
Fukunaga
Yoshitaka
Y
D002675:Child, Preschool; D005260:Female; D005776:Gaucher Disease / Q000188:drug therapy*; D005962:Glucosylceramidase / Q000627:therapeutic use*; D018575:Home Care Services, Hospital-Based; D006801:Humans; D011994:Recombinant Proteins / Q000627:therapeutic use*
D011994:Recombinant Proteins; D005962:Glucosylceramidase; C090568:imiglucerase