Gene therapy for hemophilia: are viral vectors really feasible?
Walsh
C
C
Mount Sinai School of Medicine, New York City, New York 10029, USA. christopher.e.walsh@mssm.edu
D000818:Animals; D000229:Dependovirus / Q000235:genetics; D004285:Dogs; D005164:Factor IX / Q000235:genetics; D005169:Factor VIII / Q000235:genetics; D015316:Genetic Therapy / Q000009:adverse effects / Q000379:methods; D005822:Genetic Vectors; D006467:Hemophilia A / Q000628:therapy*; D002836:Hemophilia B / Q000628:therapy; D006801:Humans; D008297:Male; D051379:Mice; D012449:Safety
D005169:Factor VIII; D005164:Factor IX