Skipping to new gene therapies for muscular dystrophy.
Tidball
James G
JG
Spencer
Melissa J
MJ
D000818:Animals; D004195:Disease Models, Animal; D005091:Exons; D015316:Genetic Therapy; D006801:Humans; D051379:Mice; D009137:Muscular Dystrophy, Animal / Q000235:genetics / Q000628:therapy*; D020388:Muscular Dystrophy, Duchenne / Q000235:genetics / Q000628:therapy*; D020320:Oligoribonucleotides, Antisense; D012313:RNA / Q000235:genetics / Q000378:metabolism*; D012326:RNA Splicing
D020320:Oligoribonucleotides, Antisense; D012313:RNA