title: Skipping to new gene therapies for muscular dystrophy.
authors.forename: James G
authors.initials: JG
authors.lastname: Tidball
authors.forename: Melissa J
authors.initials: MJ
authors.lastname: Spencer
mesh_terms: D000818:Animals; D004195:Disease Models, Animal; D005091:Exons; D015316:Genetic Therapy; D006801:Humans; D051379:Mice; D009137:Muscular Dystrophy, Animal / Q000235:genetics / Q000628:therapy*; D020388:Muscular Dystrophy, Duchenne / Q000235:genetics / Q000628:therapy*; D020320:Oligoribonucleotides, Antisense; D012313:RNA / Q000235:genetics / Q000378:metabolism*; D012326:RNA Splicing
chemical_list: D020320:Oligoribonucleotides, Antisense; D012313:RNA