Efficient and specific repair of sickle beta-globin RNA by trans-splicing ribozymes.
D000755:Anemia, Sickle Cell / Q000097:blood* / Q000628:therapy; D001483:Base Sequence; D005914:Globins / Q000235:genetics*; D006801:Humans; D007438:Introns; D008969:Molecular Sequence Data; D009154:Mutation; D009690:Nucleic Acid Conformation; D016133:Polymerase Chain Reaction; D012313:RNA / Q000737:chemistry / Q000235:genetics* / Q000378:metabolism; D016337:RNA, Catalytic / Q000235:genetics / Q000378:metabolism*; D012689:Sequence Homology, Nucleic Acid; D020040:Trans-Splicing; D014162:Transfection
D016337:RNA, Catalytic; D012313:RNA; D005914:Globins