title: Good things come in small packages for hemophilia.
authors.affiliation: Department of Biological Chemistry, Howard Hughes Medical Institute, University of Michigan Medical Center, Ann Arbor, MI 48109-0650, USA. kaufmanr@umich.edu
authors.forename: R J
authors.initials: RJ
authors.lastname: Kaufman
mesh_terms: D000818:Animals; D005169:Factor VIII / Q000008:administration & dosage* / Q000627:therapeutic use; D015316:Genetic Therapy; D006412:Hematopoietic Stem Cells / Q000166:cytology / Q000378:metabolism; D006467:Hemophilia A / Q000188:drug therapy*; D006801:Humans; D008533:Megakaryocytes / Q000166:cytology / Q000378:metabolism / Q000637:transplantation; D014161:Transduction, Genetic; D014841:von Willebrand Factor / Q000008:administration & dosage / Q000502:physiology
chemical_list: D014841:von Willebrand Factor; D005169:Factor VIII