New approaches to treat PKU: how far are we?
Blau
Nenad
N
Department of Pediatrics, University of Zürich, Switzerland. Nenad.Blau@kispi.unizh.ch
Scriver
Charles R
CR
D000818:Animals; D001708:Biopterins / Q000031:analogs & derivatives* / Q000627:therapeutic use; D015316:Genetic Therapy; D006801:Humans; D051379:Mice; D010650:Phenylalanine Ammonia-Lyase / Q000235:genetics / Q000378:metabolism; D010661:Phenylketonurias / Q000628:therapy*
D001708:Biopterins; D010650:Phenylalanine Ammonia-Lyase; C003402:sapropterin