Effective treatment of the central nervous system in lysosomal storage diseases: save that brain!
Peters
Charles
C
D000818:Animals; D016026:Bone Marrow Transplantation; D002493:Central Nervous System Diseases / Q000628:therapy*; D015316:Genetic Therapy; D006801:Humans; D020140:Lysosomal Storage Diseases, Nervous System / Q000628:therapy*