Phase I trial of intramuscular injection of a recombinant adeno-associated virus alpha 1-antitrypsin (rAAV2-CB-hAAT) gene vector to AAT-deficient adults.
D000328:Adult; D000818:Animals; D002985:Clinical Protocols; D000229:Dependovirus; D015316:Genetic Therapy; D005822:Genetic Vectors / Q000008:administration & dosage; D006801:Humans; D007273:Injections, Intramuscular; D051379:Mice; D000515:alpha 1-Antitrypsin / Q000235:genetics* / Q000378:metabolism; D019896:alpha 1-Antitrypsin Deficiency / Q000188:drug therapy*
D000515:alpha 1-Antitrypsin