title: Targeted conversion of the transthyretin gene in vitro and in vivo.
mesh_terms: D017772:Amyloid Neuropathies / Q000235:genetics / Q000628:therapy*; D000818:Animals; D001483:Base Sequence; D003094:Collagen / Q000235:genetics; D004260:DNA Repair / Q000235:genetics; D005785:Gene Conversion; D018390:Gene Targeting / Q000379:methods*; D015316:Genetic Therapy / Q000379:methods*; D006801:Humans; D008099:Liver / Q000378:metabolism; D051379:Mice; D008810:Mice, Inbred C57BL; D008822:Mice, Transgenic; D008969:Molecular Sequence Data; D009841:Oligonucleotides / Q000235:genetics; D011228:Prealbumin / Q000235:genetics*; D014162:Transfection
chemical_list: D009841:Oligonucleotides; D011228:Prealbumin; C059821:atelocollagen; D003094:Collagen