Advances in the treatment of mucopolysaccharidosis type I.
Muenzer
Joseph
J
Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, USA.
Fisher
Amy
A
D016026:Bone Marrow Transplantation; D005312:Fetal Blood / Q000637:transplantation*; D018380:Hematopoietic Stem Cell Transplantation; D006801:Humans; D008247:Lysosomes / Q000201:enzymology; D008360:Mannosephosphates / Q000378:metabolism; D008059:Mucopolysaccharidosis I / Q000201:enzymology / Q000628:therapy*
D008360:Mannosephosphates; C027693:mannose-6-phosphate